Rare Kidney Diseases that Now Have Treatments

In the past, most rare kidney disease had no recognized or targeted treatments. Here are a collection of rare kidney diseases that have available treatments.

1. Autosomal Dominant Polycystic Kidney Disease (ADPKD)

Tolvaptan

2. atypical hemolytic uremic syndrome (aHUS) or complement-mediated thrombotic microangiopathy

Eculizumab

3. ANCA vasculitis

Treatments include corticosteroids, cyclophosphamide, rituximab, azathioprine, mycophenolate, avacopan (C5a receptor antagonist)